If you want to make a company based off a science discovery you have to start by replicating the initial discovery. Most biotech companies die there.
You don't move a drug into clinical trials unless you can replicate the initial studies, which is almost always "drug x cures y in animal z."
They die when they try to determine if "drug x cures y in humans."
LOL. That is often the hard part. "We cured your toe fungus. Sorry about the heart attack."