Pfizer scores FDA nod for hemophilia B gene therapy, will charge $3.5M per dose

fiercepharma.com

2 pointsOzarkian1 comment

”Hemophilia B is a rare genetic disorder that prevents normal blood clotting for people who can’t generate the factor IX (FIX) protein. According to the World Federation of Hemophilia, 38,000 people have the disorder.”

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